Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...
A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...
The need to change regulations around gene-editing treatments was endorsed in November by the head of the US Food and Drug ...
The Phase 1/2 trial is a first-in-human, open-label, multi-national study designed to evaluate the safety, tolerability, and efficacy of TSRA-196 in adults with AATD. Trial participants will receive a ...
A new CRISPR breakthrough shows scientists can turn genes back on without cutting DNA, by removing chemical tags that act ...
Beam stock launched Monday after the company reached a deal with the Food and Drug Administration for its gene-editing drug, ...
He Jiankui spent three years in prison after creating gene-edited babies. Now back at work, he sees a greater opening for ...
Victoria Gray spent 34 years battling the debilitating pain of sickle cell disease. Then she volunteered to be the world's first "prototype" for a CRISPR therapy, based on technology invented at UC ...
Baby KJ was the first to receive a bespoke gene-editing treatment. Personalized drugs for others could be approved within the ...
"Regulatory flexibility must be tailored for cell and gene therapies," commented FDA Commissioner Marty Makary. "These are ...
Like other developing countries, Indonesia is facing a familiar dilemma: how to feed a growing population while protecting ...